Successful treatment of transfusion-dependent β-thalassemia: multiple paths to reach potential cure
Signal Transduct Target Ther
.
2025 Feb 17;10(1):55.
doi: 10.1038/s41392-025-02135-9.
Authors
Michael Morgan
1
2
,
Axel Schambach
3
4
5
Affiliations
1
Institute of Experimental Hematology, Hannover Medical School, Hannover, 30625, Germany.
2
REBIRTH Research Center for Translational Regenerative Medicine, Hannover Medical School, Hannover, 30625, Germany.
3
Institute of Experimental Hematology, Hannover Medical School, Hannover, 30625, Germany. schambach.axel@mh-hannover.de.
4
REBIRTH Research Center for Translational Regenerative Medicine, Hannover Medical School, Hannover, 30625, Germany. schambach.axel@mh-hannover.de.
5
Division of Hematology / Oncology, Boston Children's Hospital, Harvard Medical School, Boston, MA, 02115, USA. schambach.axel@mh-hannover.de.
PMID:
39956809
PMCID:
PMC11830765
DOI:
10.1038/s41392-025-02135-9
No abstract available
Grants and funding
REBIRTH/Niedersächsisches Ministerium für Wissenschaft und Kultur (Ministry for Science and Culture of Lower Saxony)