Multi-omic analysis of SDHB-deficient pheochromocytomas and paragangliomas identifies metastasis and treatment-related molecular profiles

Nat Commun. 2025 Mar 17;16(1):2632. doi: 10.1038/s41467-025-57595-y.

Abstract

Hereditary SDHB-mutant pheochromocytomas (PC) and paragangliomas (PG) are rare tumours with a high propensity to metastasize although their clinical behaviour is unpredictable. To characterize the genomic landscape of these tumours and identify metastasis biomarkers, we perform multi-omic analysis on 94 tumours from 79 patients using seven molecular methods. Sympathetic (chromaffin cell) and parasympathetic (non-chromaffin cell) PCPG have distinct molecular profiles reflecting their cell-of-origin and biochemical profile. TERT and ATRX-alterations are associated with metastatic PCPG and these tumours have an increased mutation load, and distinct transcriptional and telomeric features. Most PCPG have quiet genomes with some rare co-operative driver events, including EPAS1/HIF-2α mutations. Two mechanisms of acquired resistance to DNA alkylating chemotherapies are identifiable; MGMT overexpression and mismatch repair-deficiency causing hypermutation. Our comprehensive multi-omic analysis of SDHB-mutant PCPG therefore identifies features of metastatic disease and treatment response, expanding our understanding of these rare neuroendocrine tumours.

MeSH terms

  • Adrenal Gland Neoplasms* / drug therapy
  • Adrenal Gland Neoplasms* / genetics
  • Adrenal Gland Neoplasms* / pathology
  • Adult
  • Aged
  • Basic Helix-Loop-Helix Proteins / genetics
  • Biomarkers, Tumor / genetics
  • DNA Modification Methylases
  • DNA Repair Enzymes / genetics
  • DNA Repair Enzymes / metabolism
  • Endothelial PAS Domain-Containing Protein 1
  • Female
  • Humans
  • Male
  • Middle Aged
  • Multiomics
  • Mutation
  • Neoplasm Metastasis
  • Paraganglioma* / drug therapy
  • Paraganglioma* / genetics
  • Paraganglioma* / pathology
  • Pheochromocytoma* / drug therapy
  • Pheochromocytoma* / genetics
  • Pheochromocytoma* / pathology
  • Succinate Dehydrogenase* / deficiency
  • Succinate Dehydrogenase* / genetics
  • Telomerase / genetics
  • Telomerase / metabolism
  • Tumor Suppressor Proteins
  • X-linked Nuclear Protein

Substances

  • Succinate Dehydrogenase
  • Telomerase
  • DNA Repair Enzymes
  • Basic Helix-Loop-Helix Proteins
  • Biomarkers, Tumor
  • X-linked Nuclear Protein
  • DNA Modification Methylases
  • Tumor Suppressor Proteins
  • Endothelial PAS Domain-Containing Protein 1
  • SDHB protein, human
  • TERT protein, human
  • ATRX protein, human
  • MGMT protein, human