Oral esketamine for patients with severe treatment-resistant depression: Effectiveness, safety, and tolerability of a six-week open-label treatment program

J Psychopharmacol. 2025 Jun;39(6):559-570. doi: 10.1177/02698811251332831. Epub 2025 Apr 25.

Abstract

Background: Oral esketamine for patients with treatment-resistant depression (TRD) could offer certain advantages over other routes, such as intravenous or intranasal, but it has not been systematically studied in a real-world setting.

Aims: Here we present results from a relatively large naturalistic study to evaluate the effectiveness, tolerability, and safety of oral esketamine in patients with TRD.

Methods: One hundred eighty-five adults with severe TRD (average of 8.1 antidepressant trials plus electroconvulsive therapy in 63% without beneficial outcome) received oral esketamine treatment twice-weekly for 6 weeks with individually titrated doses ranging from 0.5 to 3 mg/kg. Outcome measures included change from baseline to week 6 on the Hamilton Depression Rating Scale (HDRS17), Minimal Clinically Important Difference (MCID), response, remission, self-reported symptom improvement, functioning, and side effects.

Results: Oral esketamine treatment improved depressive symptom severity on the HDRS17 from 21.2 to 15.8 (p < 0.001). MCID, response, and remission rates were 47.1%, 26.8% and 15.6% respectively. In 45.9% of participants, treatment was continued after 6 weeks to maintain initial positive effects. Side effects were reported frequently but were overall well tolerated. The drop-out rate was 7.6%. We found no significant adverse effects associated with urinary tract or cognition.

Conclusions: Repeated treatment with oral esketamine is effective in improving depressive symptom severity in highly treatment-resistant depressive patients. It is safe, well tolerated, and patient-friendly. Considering the level of treatment resistance, outcomes were in the range of studies investigating other routes of (es)ketamine administration.

Keywords: Treatment-resistant depression; oral esketamine; real-world effectiveness.

MeSH terms

  • Administration, Oral
  • Adult
  • Aged
  • Antidepressive Agents* / administration & dosage
  • Antidepressive Agents* / adverse effects
  • Antidepressive Agents* / therapeutic use
  • Depressive Disorder, Treatment-Resistant* / drug therapy
  • Electroconvulsive Therapy / methods
  • Female
  • Humans
  • Ketamine* / administration & dosage
  • Ketamine* / adverse effects
  • Ketamine* / therapeutic use
  • Male
  • Middle Aged
  • Psychiatric Status Rating Scales
  • Severity of Illness Index
  • Treatment Outcome

Substances

  • Ketamine
  • Esketamine
  • Antidepressive Agents