Modeling Cystic Fibrosis Patient-Specific Responses to CFTR Modulators Using Human Induced Pluripotent Stem Cells
Am J Respir Crit Care Med
.
2025 Oct;211(10):1970-1972.
doi: 10.1164/rccm.202502-0467RL.
Authors
Kayshani R Kanagarajah
1
2
,
Ming Jia Michael Wu
1
,
Timothy Lam
1
,
Henry T Quach
1
2
,
Rasha Salih
1
2
,
Krista Antonio
1
2
,
Theo J Moraes
3
,
Felix Ratjen
3
,
Christine E Bear
4
,
Amy P Wong
1
2
Affiliations
1
Program in Developmental and Stem Cell Biology.
2
Department of Laboratory Medicine & Pathobiology, University of Toronto, Toronto, Ontario, Canada.
3
Program in Translational Medicine, Hospital for Sick Children, Toronto, Ontario, Canada; and.
4
Program in Molecular Medicine, and.
PMID:
40548910
PMCID:
PMC12555047
DOI:
10.1164/rccm.202502-0467RL
No abstract available
Publication types
Letter
Grants and funding
OGI-148/Genome Canada and Ontario Genomics Institute LSARP/United States
2022-04836/Natural Sciences and Engineering Research Council of Canada/United States
Cystic Fibrosis Canada/United States
Sick Kids Foundation/United States