Multimodal analysis of cell-free DNA enhances differentiation of early-stage breast cancer from benign lesions and healthy individuals

BMC Biol. 2025 Aug 20;23(1):259. doi: 10.1186/s12915-025-02371-z.

Abstract

Background: Breast cancer (BC) remains the second leading cause of cancer-related mortality among women worldwide. Liquid biopsy based on circulating tumor DNA (ctDNA) offers a promising noninvasive approach for early detection; however, differentiating malignant tumors from benign abnormalities remains a significant challenge.

Results: Here, we developed a multimodal approach to analyze cfDNA methylation and fragmentomic patterns in 273 BC patients, 108 individuals with benign breast conditions, and 134 healthy controls. Genome-wide analyses revealed distinct cfDNA copy number alterations and cytosine-enriched cleavage sites in BC patients. Targeted sequencing further revealed unique methylation patterns, including hypermethylation in GPR126, KLF3, and TLR10 and hypomethylation in TOP1 and MAFB. Our machine-learning model achieved an AUC of 0.90, with 93.6% specificity and 62.1-66.3% sensitivity for stage I-II cancers. In symptomatic populations, sensitivities were 50.0%, 68.2%, and 64.7% for BI-RADS categories 3, 4, and 5, respectively, with 96.1% specificity.

Conclusions: These findings underscore the potential of cfDNA biomarkers to enhance BC detection and reduce the rate of unnecessary biopsies.

Keywords: Benign abnormalities; Breast cancer; CfDNA; Methylation and fragmentomic.

MeSH terms

  • Adult
  • Aged
  • Biomarkers, Tumor / genetics
  • Breast Neoplasms* / blood
  • Breast Neoplasms* / diagnosis
  • Breast Neoplasms* / genetics
  • Breast Neoplasms* / pathology
  • Cell-Free Nucleic Acids* / genetics
  • DNA Methylation
  • Early Detection of Cancer / methods
  • Female
  • Humans
  • Middle Aged

Substances

  • Cell-Free Nucleic Acids
  • Biomarkers, Tumor