Engineering mRNA CAR-T Cells for Cancer Immunotherapy

Methods Mol Biol. 2025:2965:285-321. doi: 10.1007/978-1-0716-4742-4_14.

Abstract

Adoptive T-cell therapy is a promising cancer immunotherapy, but isolating tumor-specific cytotoxic T cells is time-consuming and often unsuccessful. An alternative approach involves genetically modifying T cells to express tumor antigen-specific T-cell receptors (TCRs) or chimeric antigen receptors (CARs), enabling the redirection of large numbers of immune cells to target malignant cells. CARs combine the specificity of antibody-derived single-chain variable fragments with T-cell signaling domains (e.g., CD3ζ, CD28, 4-1BB), enabling T cells to recognize and kill antigen-positive cancer cells in an MHC-independent manner. This chapter outlines protocols for large-scale T-cell expansion and medium-scale production of messenger RNA (mRNA) CAR-T cells using electroporation as a delivery method. Two CARs are used as model systems: one targeting CD19 and another targeting an antigen expressed on hematological malignancies and solid tumors.

Keywords: Chimeric antigen receptor; Gene therapy; T lymphocytes; mRNA electroporation.

MeSH terms

  • Antigens, CD19 / immunology
  • Electroporation
  • Humans
  • Immunotherapy, Adoptive* / methods
  • Neoplasms* / immunology
  • Neoplasms* / therapy
  • RNA, Messenger* / genetics
  • Receptors, Antigen, T-Cell* / genetics
  • Receptors, Antigen, T-Cell* / immunology
  • Receptors, Chimeric Antigen* / genetics
  • Receptors, Chimeric Antigen* / immunology
  • Receptors, Chimeric Antigen* / metabolism
  • T-Lymphocytes* / immunology
  • T-Lymphocytes* / metabolism

Substances

  • Receptors, Chimeric Antigen
  • RNA, Messenger
  • Receptors, Antigen, T-Cell
  • Antigens, CD19