Background: Hypertrophic cardiomyopathy (HCM) is typically linked to dominant variants in sarcomeric genes, but rare minor genes, including TRIM63 coding for an E3 ubiquitin-protein ligase, have recently emerged as potential causes of recessive HCM.
Methods and results: Among 517 adult patients with clinical HCM who underwent next-generation sequencing, we found six index cases carrying biallelic TRIM63 variants-four homozygous and two compound heterozygous. They presented with early-onset disease, marked concentric hypertrophy, diffuse myocardial fibrosis, and progressive left ventricular dysfunction. One patient underwent heart transplantation. No cardiac disease was found in heterozygous relatives.
Conclusions: TRIM63-related HCM is rare but clinically distinct. Early identification of TRIM63 homozygous and two compound heterozygous variants in HCM is crucial and warrants proactive clinical surveillance.
Keywords: Autosomal recessive; Genetic testing; Hypertrophic cardiomyopathy; Minor genes; TRIM63 gene.
Copyright © 2025 The Authors. Published by Elsevier B.V. All rights reserved.