Expanding indications and developmental landscape of HER2-targeted therapies in breast cancer: a pharmacotherapeutic perspective

Expert Opin Pharmacother. 2025 Dec;26(17):1855-1865. doi: 10.1080/14656566.2025.2591813. Epub 2025 Nov 19.

Abstract

Introduction: This review provides an updated overview of the evolving pharmacologic landscape of human epidermal growth factor receptor 2 (HER2)-targeted therapies in breast cancer, highlighting key clinical trial data, recent indication expansions, resistance mechanisms, and emerging therapeutic agents in development.

Areas covered: This review draws on a comprehensive literature search of published studies and major oncology conference proceedings, focusing primarily on data from key phase III clinical trials of HER2-targeted therapies. Studies published within the past decade that have influenced current standards of care were prioritized.

Expert opinion: The treatment paradigm for HER2-expressing breast cancer is evolving rapidly. Trastuzumab deruxtecan has redefined management for both HER2-positive and the newly recognized HER2-low subgroups, while tucatinib offers a critical systemic option for central nervous system metastases. Optimal sequencing and resistance management remain critical challenges in this dynamic field. Nonetheless, HER2-targeted pharmacotherapy continues to advance rapidly, driven by innovative drug designs and strategic clinical developments.

Keywords: Breast cancer; HER2; antibody-drug conjugate; bispecific antibody; clinical trials; metastatic disease; pharmacotherapy; tyrosine kinase inhibitor.

Publication types

  • Review

MeSH terms

  • Animals
  • Antineoplastic Agents* / pharmacology
  • Antineoplastic Agents* / therapeutic use
  • Breast Neoplasms* / drug therapy
  • Breast Neoplasms* / pathology
  • Camptothecin / analogs & derivatives
  • Drug Design
  • Drug Development
  • Drug Resistance, Neoplasm
  • Erb-b2 Receptor Tyrosine Kinases* / antagonists & inhibitors
  • Erb-b2 Receptor Tyrosine Kinases* / metabolism
  • Female
  • Humans
  • Immunoconjugates / administration & dosage
  • Immunoconjugates / pharmacology
  • Immunoconjugates / therapeutic use
  • Molecular Targeted Therapy*
  • Trastuzumab

Substances

  • Erb-b2 Receptor Tyrosine Kinases
  • Antineoplastic Agents
  • Trastuzumab
  • Immunoconjugates
  • Camptothecin
  • ERBB2 protein, human
  • trastuzumab deruxtecan