Innovative treatment approaches for paediatric obsessive-compulsive disorder

Expert Opin Pharmacother. 2025 Dec;26(17):1763-1784. doi: 10.1080/14656566.2025.2591073. Epub 2025 Nov 24.

Abstract

Introduction: Pediatric obsessive-compulsive disorder is a chronic and often under-diagnosed condition with onset in childhood or adolescence, leading to marked functional impairment. While current first-line treatments, cognitive-behavioral therapy and selective serotonin reuptake inhibitors, are effective in many cases, a substantial proportion of patients remain refractory, especially those with early onset.

Areas covered: This review explores the emerging etiopathogenetic models of pediatric OCD, emphasizing neurodevelopmental, glutamatergic, and immune-inflammatory mechanisms. A literature search was conducted using PubMed and ClinicalTrials.gov, focusing on controlled and observational studies on pediatric OCD, including novel therapeutic targets. Special attention is given to the PANDAS/PANS subgroup, which has helped shift the paradigm beyond monoaminergic dysfunction. New pharmacological strategies, such as glutamate modulators and anti-inflammatory agents, are critically examined alongside established psychotherapeutic approaches.

Expert opinion: OCD remains the only psychiatric disorder in which a childhood syndrome, PANDAS, has led to immune-based hypotheses that influenced adult research and treatment. Despite promising signals from small trials and case studies, robust pediatric data are scarce. Future efforts should prioritize large-scale, age-specific trials, early stratification based on immune profiles, and mechanistically guided interventions to advance personalized care in pediatric OCD.

Keywords: PANDAS; PANS; Pediatric OCD; SSRI; cognitive-behavioral therapy; glutamate; immune system; treatment resistance.

Publication types

  • Review

MeSH terms

  • Adolescent
  • Animals
  • Anti-Inflammatory Agents / therapeutic use
  • Child
  • Cognitive Behavioral Therapy / methods
  • Humans
  • Obsessive-Compulsive Disorder* / drug therapy
  • Obsessive-Compulsive Disorder* / physiopathology
  • Obsessive-Compulsive Disorder* / therapy
  • Selective Serotonin Reuptake Inhibitors / therapeutic use

Substances

  • Selective Serotonin Reuptake Inhibitors
  • Anti-Inflammatory Agents