Hexokinase 2-mediated histone H3K18la promotes PAI-1-dependent thrombosis in acute myeloid leukemia via tumor-endothelial crosstalk

Nat Commun. 2025 Nov 19;16(1):10168. doi: 10.1038/s41467-025-65259-0.

Abstract

Acute myeloid leukemia is an aggressive hematological malignancy frequently complicated by coagulation disorders, including thrombosis and hemorrhage, which contribute to poor outcomes. Here, we identify lactate-driven histone lactylation as a mechanism promoting thrombosis in acute myeloid leukemia. We demonstrate that hexokinase 2-mediated glycolysis in leukemic cells leads to lactate accumulation, which enhances histone H3 lysine 18 lactylation and upregulates plasminogen activator inhibitor-1 expression, impairing fibrinolysis. Lactate released by acute myeloid leukemia cells is internalized by vascular endothelial cells via monocarboxylate transporter 1, amplifying plasminogen activator inhibitor-1 expression and thrombotic risk. Inhibition of hexokinase 2-mediated lactate production or monocarboxylate transporter 1-mediated lactate uptake attenuates thrombosis. Our findings reveal a critical link between tumor metabolism, epigenetic modifications, and coagulation dysfunction in acute myeloid leukemia.

MeSH terms

  • Animals
  • Cell Line, Tumor
  • Endothelial Cells / metabolism
  • Fibrinolysis
  • Glycolysis
  • Hexokinase* / genetics
  • Hexokinase* / metabolism
  • Histones* / metabolism
  • Human Umbilical Vein Endothelial Cells
  • Humans
  • Lactic Acid / metabolism
  • Leukemia, Myeloid, Acute* / complications
  • Leukemia, Myeloid, Acute* / genetics
  • Leukemia, Myeloid, Acute* / metabolism
  • Leukemia, Myeloid, Acute* / pathology
  • Mice
  • Monocarboxylic Acid Transporters / metabolism
  • Plasminogen Activator Inhibitor 1* / genetics
  • Plasminogen Activator Inhibitor 1* / metabolism
  • Thrombosis* / genetics
  • Thrombosis* / metabolism
  • Thrombosis* / pathology

Substances

  • Hexokinase
  • Histones
  • Plasminogen Activator Inhibitor 1
  • HK2 protein, human
  • Lactic Acid
  • SERPINE1 protein, human
  • Monocarboxylic Acid Transporters