Immunological profile of the tumor immune microenvironment of upper tract urothelial carcinoma predicts recurrence patterns

Cancer Immunol Immunother. 2026 Jan 27;75(2):41. doi: 10.1007/s00262-025-04254-2.

Abstract

Background: The association between the tumor immune microenvironment (TiME) in upper tract urothelial carcinoma (UTUC) and its prognosis remains unclear. We investigated the relationship between TiME and UTUC recurrence patterns.

Methods: We evaluated 90 patients who underwent nephroureterectomy for UTUC and divided them into nonrecurrence, distant metastasis, and intravesical recurrence-only groups. We assessed the association of the TiME with clinicopathological factors using surgical tissues and the prognosis of the three groups via multiplex fluorescence immunohistochemistry.

Results: The median age was 71 years (44-89), and 58 (64%) were male. Intratumoral CD4+ T cell density was significantly higher in the nonrecurrence group (p = 0.0004) than the other groups, whereas intra- and peritumoral regulatory T cell (Treg; CD3+CD4+FoxP3+ cell) density was higher in the distant metastases group than the intravesical recurrence-only group (p = 0.0025). In the multivariate analysis, pathological T stage and CD4+ T cells, and pathological T stage and Treg were independent predictors of recurrence-free survival (p = 0.045, p = 0.017) and metastatic-free survival (p = 0.027, p = 0.011), respectively.

Conclusions: Our study demonstrated that CD4+ T cells and Tregs in the TiME of patients with UTUC were independent predictors of high-risk recurrence together with high pathological stage. The analysis of TiME in surgical specimens may provide an objective indicator of the efficacy of adjuvant therapy in UTUC.

Keywords: Distant metastasis; Nephroureterectomy; Regulatory T cell; Tumor immune microenvironment; Upper tract urothelial carcinoma.

MeSH terms

  • Adult
  • Aged
  • Aged, 80 and over
  • Carcinoma, Transitional Cell* / immunology
  • Carcinoma, Transitional Cell* / pathology
  • Female
  • Humans
  • Male
  • Middle Aged
  • Neoplasm Recurrence, Local* / immunology
  • Neoplasm Recurrence, Local* / pathology
  • Prognosis
  • T-Lymphocytes, Regulatory / immunology
  • Tumor Microenvironment* / immunology
  • Urologic Neoplasms* / immunology
  • Urologic Neoplasms* / pathology