Impact of prior immune checkpoint inhibitor on trastuzumab deruxtecan in HER2-positive advanced gastric cancer: exploratory analysis of the EN-DEAVOR study

Jpn J Clin Oncol. 2026 May 7;56(5):538-545. doi: 10.1093/jjco/hyaf216.

Abstract

Background: Human epidermal growth factor receptor 2 (HER2)-positive advanced gastric cancer (AGC) presents significant therapeutic challenges due to its molecular heterogeneity. Previous studies suggest that immune checkpoint inhibitors (ICIs) may enhance the efficacy of subsequent HER2-targeted therapy. However, evidence suggesting an optimal sequence for nivolumab and trastuzumab deruxtecan (T-DXd) treatment is limited. This exploratory analysis of EN-DEAVOR evaluated the effectiveness and safety of administering T-DXd relative to the timing of prior ICI administration.

Methods: This study assessed real-world outcomes of T-DXd in patients with HER2-positive AGC stratified by prior ICI exposure: within 2 months of nivolumab (Group A), >2 months (Group B), and no prior nivolumab (Group C). The primary effectiveness endpoints included real-world progression-free survival (rwPFS) and objective response rate (ORR). Safety endpoints included grade ≥ 3 adverse events (AEs).

Results: Among 311 eligible patients, Group A showed the longest median rwPFS (n = 63; 6.9 months) compared with Group B (n = 63; 4.6 months) and Group C (n = 185; 4.2 months). The risk of progression was significantly lower in Group A compared with Group B (hazard ratio [95% confidence interval]: 0.6 [0.4-0.9]; P = .0074). ORR was numerically highest in Group A (54.9%) versus Group B (30.8%) and Group C (43.4%). More patients in Group B (58.7%) experienced grade ≥ 3 AEs than in Group A (50.8%) and Group C (43.8%). No new safety signals were observed.

Conclusions: Initiating T-DXd within 2 months post-ICI may enhance therapeutic efficacy in HER2-positive AGC without affecting safety, supporting a potential sequencing option after ICI therapy.

Keywords: EN-DEAVOR; HER2-positive gastric cancer; nivolumab; trastuzumab deruxtecan; treatment strategy.

MeSH terms

  • Adult
  • Aged
  • Aged, 80 and over
  • Antineoplastic Combined Chemotherapy Protocols* / therapeutic use
  • Camptothecin* / administration & dosage
  • Camptothecin* / analogs & derivatives
  • Camptothecin* / therapeutic use
  • Erb-b2 Receptor Tyrosine Kinases* / metabolism
  • Female
  • Humans
  • Immune Checkpoint Inhibitors* / administration & dosage
  • Immune Checkpoint Inhibitors* / pharmacology
  • Immune Checkpoint Inhibitors* / therapeutic use
  • Immunoconjugates* / administration & dosage
  • Immunoconjugates* / therapeutic use
  • Male
  • Middle Aged
  • Stomach Neoplasms* / drug therapy
  • Stomach Neoplasms* / pathology
  • Trastuzumab* / administration & dosage
  • Trastuzumab* / pharmacology
  • Trastuzumab* / therapeutic use

Substances

  • Trastuzumab
  • Immune Checkpoint Inhibitors
  • Erb-b2 Receptor Tyrosine Kinases
  • trastuzumab deruxtecan
  • ERBB2 protein, human
  • Immunoconjugates
  • Camptothecin