Mutant calreticulin-directed immunotherapies in myeloproliferative neoplasms

Blood Neoplasia. 2026 Jan 14;3(2):100193. doi: 10.1016/j.bneo.2026.100193. eCollection 2026 May.

Abstract

Mutations in calreticulin (CALR) represent the second most common oncogenic driver of myeloproliferative neoplasms. CALR mutations result in the introduction of a neomorphic C-terminal tail that is absent from the normal proteome, which has positioned it as a compelling target for immunotherapeutic intervention. Early studies have demonstrated mutant CALR can elicit T-cell responses, laying the foundation for efforts to exploit this vulnerability through vaccines, antibody-based strategies, and T-cell-based therapies. Here, we summarize the current understanding of normal and mutant CALR biology, discuss progress in developing CALR-directed immunotherapies, and highlight the challenges and opportunities for translating these approaches into the clinic.

Publication types

  • Review