Cytidinyl/Cationic Lipids-siRNA Delivery Silences MYC to Reprogram Macrophages and Circadian Rhythm for Cancer Treatment

Mol Pharm. 2026 Apr 6;23(4):2597-2610. doi: 10.1021/acs.molpharmaceut.5c01718. Epub 2026 Mar 17.

Abstract

Nonsmall cell lung cancer (NSCLC) remains a leading cause of cancer-related mortality, with MYC oncogene overexpression driving tumor progression and immunosuppression. MYC has been deemed "undruggable" for a long period, and the impact of its silencing on the tumor associated macrophage polarization and circadian rhythm remains unexplored. Here, we developed a lipid nanoparticle (siMYC@Dmix) composed of cytidinyl lipid (DNCA), gemini-like cationic lipid (CLD), and DSPE-PEG2000 for efficient MYC siRNA delivery. In vitro, siMYC@Dmix showed robust cellular uptake, lysosomal escape, and ∼77% MYC mRNA silencing in Lewis Lung Carcinoma (LLC) cells. In vivo, siMYC@Dmix treatment significantly inhibited tumor growth in C57BL/6J mice and induced a profound remodeling of the tumor immune microenvironment. This was characterized by a shift in macrophage polarization toward the M1 phenotype, increased infiltration and cytotoxic function of CD8+ T cells, enhanced natural killer (NK) cell activity, and maturation of dendritic cells (DCs). Crucially, MYC silencing restored the expression of core circadian clock genes. Our findings unveil a promising RNAi-based strategy that concurrently targets MYC-driven tumorigenesis, corrects circadian dysfunction, and reinstates antitumor immunity, presenting a multifaceted therapeutic approach for NSCLC.

Keywords: MYC silencing; cancer therapy; circadian clock; cytidinyl lipid; tumor immune microenvironment.

MeSH terms

  • Animals
  • Carcinoma, Lewis Lung / genetics
  • Carcinoma, Non-Small-Cell Lung* / genetics
  • Carcinoma, Non-Small-Cell Lung* / therapy
  • Cations / chemistry
  • Cell Line, Tumor
  • Circadian Rhythm* / drug effects
  • Circadian Rhythm* / genetics
  • Dendritic Cells
  • Gene Silencing
  • Humans
  • Lipids* / chemistry
  • Lung Neoplasms* / genetics
  • Lung Neoplasms* / therapy
  • Macrophages* / metabolism
  • Mice
  • Mice, Inbred C57BL
  • Nanoparticles / chemistry
  • Proto-Oncogene Proteins c-myc* / genetics
  • RNA, Small Interfering* / administration & dosage
  • RNA, Small Interfering* / genetics
  • Tumor Microenvironment / drug effects

Substances

  • RNA, Small Interfering
  • Proto-Oncogene Proteins c-myc
  • Lipids
  • Myc protein, mouse
  • Cations