PD-1 blockade plus tyrosine kinase inhibitor remodels the tumor microenvironment in advanced renal cell carcinoma

Nat Commun. 2026 Mar 31;17(1):4626. doi: 10.1038/s41467-026-70978-z.

Abstract

The combination of tyrosine kinase inhibitors (TKIs) and immune checkpoint inhibitors (ICIs) has improved clinical outcomes in advanced renal cell carcinoma (aRCC), though therapeutic resistance remains a major challenge. We conducted single-cell transcriptomic analysis on 61 tumor samples from 34 aRCC patients treated with TKIs alone or in combination with ICIs. Non-responders exhibited increased neutrophil infiltration and enrichment of SAA+ tumor cells following treatment. We identified a VEGFA+CEACAM1+ neutrophil subset exhibiting immunosuppressive properties that is associated with poor clinical response. In vivo, pharmacologic inhibition of SAA enhanced sensitivity to ICI plus TKI combination therapy, while blockade of the CEACAM1-TIM-3 axis in humanized PD-1 mouse models significantly potentiated anti-PD-1 efficacy. Our study establishes a single-cell atlas of the aRCC tumor microenvironment under treatment pressure and identifies a previously unrecognized SAA-CEACAM1-TIM-3 axis driving drug resistance, highlighting potential targets to improve therapy efficacy.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • CD8-Positive T-Lymphocytes / drug effects
  • Carcinoma, Renal Cell* / drug therapy
  • Carcinoma, Renal Cell* / genetics
  • Carcinoma, Renal Cell* / metabolism
  • Drug Resistance, Neoplasm
  • Humans
  • Immune Checkpoint Inhibitors* / pharmacology
  • Kidney Neoplasms* / drug therapy
  • Kidney Neoplasms* / genetics
  • Kidney Neoplasms* / metabolism
  • Kidney Neoplasms* / pathology
  • Ligands
  • Male
  • Mice
  • Mice, Inbred BALB C
  • Neutrophils / drug effects
  • Programmed Cell Death 1 Receptor* / antagonists & inhibitors
  • Programmed Cell Death 1 Receptor* / genetics
  • Programmed Cell Death 1 Receptor* / metabolism
  • Protein Kinase Inhibitors* / pharmacology
  • Single-Cell Analysis
  • Tumor Microenvironment* / drug effects

Substances

  • PDCD1 protein, human
  • Programmed Cell Death 1 Receptor
  • Protein Kinase Inhibitors
  • Immune Checkpoint Inhibitors
  • Ligands