An Optimized Route to the Syringolin Natural Products Enables Combinatorial Synthesis of Selective, Bioactive Inhibitors of the Plasmodium falciparum 20S Proteasome

J Med Chem. 2026 Apr 23;69(8):8897-8914. doi: 10.1021/acs.jmedchem.5c03223. Epub 2026 Apr 1.

Abstract

The syringolin natural products are covalent inhibitors of the 20S proteasome that inspire therapeutic development. Here, we report a new route to the syringolins amenable to solution and solid-phase synthesis that overcomes a problematic macrocyclization. Exploiting our synthetic approach and substrate mimicry models for proteasome inhibition by the syringolins, we generated a collection of hypothetically selective inhibitors of the Plasmodium falciparum proteasome, which is an emerging target for antimalarial drugs. We identified compounds from the library having high second-order rate constants for Plasmodium proteasome inhibition and nanomolar antiparasitic activity. They exhibited selectivity for the Plasmodium proteasome over the human proteasome. We solved cryo-EM structures of an inhibitor bound to both 20S proteasomes, revealing key contacts favoring species-selective inhibition. Together, this work provides an improved route to syringolin analogs, sheds new light on substrate mimicry by the syringolins, and provides a structural basis for the pursuit of new antimalarial drugs.

MeSH terms

  • Antimalarials* / chemical synthesis
  • Antimalarials* / chemistry
  • Antimalarials* / pharmacology
  • Biological Products* / chemical synthesis
  • Biological Products* / chemistry
  • Biological Products* / pharmacology
  • Combinatorial Chemistry Techniques
  • Cryoelectron Microscopy
  • Humans
  • Models, Molecular
  • Peptides, Cyclic* / chemical synthesis
  • Peptides, Cyclic* / chemistry
  • Peptides, Cyclic* / pharmacology
  • Plasmodium falciparum* / drug effects
  • Plasmodium falciparum* / enzymology
  • Proteasome Endopeptidase Complex* / chemistry
  • Proteasome Endopeptidase Complex* / metabolism
  • Proteasome Inhibitors* / chemical synthesis
  • Proteasome Inhibitors* / chemistry
  • Proteasome Inhibitors* / pharmacology
  • Structure-Activity Relationship

Substances

  • Proteasome Inhibitors
  • Proteasome Endopeptidase Complex
  • Antimalarials
  • Biological Products
  • Peptides, Cyclic
  • syringolin A