N-Acetylcysteine in Neurological Disorders: A Systematic Review of Clinical and Translational Evidence Across Seven Disorders

Int J Mol Sci. 2026 Mar 27;27(7):3076. doi: 10.3390/ijms27073076.

Abstract

N-acetylcysteine (NAC) is a glutathione precursor with established antioxidant and anti-inflammatory properties that has been investigated as a neuroprotective agent across multiple neurological conditions. This systematic review systematically mapped the clinical evidence for NAC across seven neurological disorders. PubMed and Cochrane Library were searched for studies published between 1 January 1995 and 31 December 2025. Twenty-three studies were included: traumatic brain injury (TBI, n = 6), Alzheimer's disease (AD, n = 5), Parkinson's disease (PD, n = 5), multiple sclerosis (n = 4), amyotrophic lateral sclerosis (n = 2), and migraine (n = 1); no eligible epilepsy studies were identified. The strongest evidence emerged for acute mild TBI, where early NAC administration significantly improved symptom resolution, and for PD, where combined intravenous/oral NAC improved dopamine transporter binding. In AD, nutraceutical formulations including NAC and other active compounds showed trends toward cognitive stabilization. Most included studies had a high or serious risk of bias, and only eight of 23 assessed oxidative stress biomarkers. NAC demonstrated a favorable safety profile across all conditions. Despite fragmented and heterogeneous evidence, the encouraging signals identified warrant large-scale randomized controlled trials with a standardized biomarker assessment.

Keywords: Alzheimer’s disease; N-acetylcysteine; Parkinson’s disease; amyotrophic lateral sclerosis; migraine; multiple sclerosis; oxidative stress; traumatic brain injury.

Publication types

  • Systematic Review
  • Review

MeSH terms

  • Acetylcysteine* / pharmacology
  • Acetylcysteine* / therapeutic use
  • Alzheimer Disease / drug therapy
  • Amyotrophic Lateral Sclerosis / drug therapy
  • Antioxidants / therapeutic use
  • Brain Injuries, Traumatic / drug therapy
  • Humans
  • Multiple Sclerosis / drug therapy
  • Nervous System Diseases* / drug therapy
  • Neuroprotective Agents* / therapeutic use
  • Oxidative Stress / drug effects
  • Parkinson Disease / drug therapy
  • Translational Research, Biomedical

Substances

  • Acetylcysteine
  • Neuroprotective Agents
  • Antioxidants