Impact of 3'-exonuclease stereoselectivity on the kinetics of phosphorothioate oligonucleotide metabolism

Antisense Nucleic Acid Drug Dev. 1998 Feb;8(1):35-42. doi: 10.1089/oli.1.1998.8.35.

Abstract

For the enzymatic digestion of a 25-mer phosphorothioate (PS) oligonucleotide, the reaction kinetics was previously determined to be the sum of two parallel processes: a fast and a very slow phase of digestion suggesting a two-exponential model. A characteristic metabolite profile was observed both in vitro and in vivo. This behavior is shown to be the result of the stereoselective cleavage of chiral R-configuration and S-configuration PS internucleotide linkages by 3'-exonucleases. The stereoselective nature of 3'-exonuclease action was analyzed by reverse-phase HPLC. The separation of eight diastereomers of the tetramer TTCT (5'-3') was used to follow the stereoselective course of exonuclease hydrolysis of PS internucleotide linkages. Degradation of the 25-mer parent compound having a 3' S-terminal internucleotide linkage was calculated to be more than 300 times slower than an analog with a 3'-terminal R-configuration. These results support an approach for protecting antisense oligonucleotides based on the chirality of only the 3'-end internucleotide linkage.

Publication types

  • Comparative Study

MeSH terms

  • Exonucleases / metabolism*
  • Hydrolysis
  • Kinetics
  • Oligonucleotides / metabolism*
  • Stereoisomerism
  • Substrate Specificity
  • Thionucleotides / metabolism*

Substances

  • Oligonucleotides
  • Thionucleotides
  • Exonucleases
  • spleen exonuclease