No abstract available
Publication types
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Research Support, Non-U.S. Gov't
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Review
MeSH terms
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Animals
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Bone Marrow Transplantation
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Central Nervous System / metabolism
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Clinical Trials as Topic
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Disease Models, Animal
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Genetic Therapy
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Humans
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Mucopolysaccharidoses / genetics
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Mucopolysaccharidoses / physiopathology
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Mucopolysaccharidoses / therapy*