Hurler syndrome: past, present, and future
J Pediatr
.
1998 Jul;133(1):7-9.
doi: 10.1016/s0022-3476(98)70170-2.
Authors
C Peters
,
E G Shapiro
,
W Krivit
PMID:
9672503
DOI:
10.1016/s0022-3476(98)70170-2
No abstract available
Publication types
Comment
Editorial
MeSH terms
Bone Marrow Transplantation*
Glycosaminoglycans / urine
Humans
Mucopolysaccharidosis I / diagnosis
Mucopolysaccharidosis I / therapy*
Quality of Life
Substances
Glycosaminoglycans