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Fosdenopterin: First Approval.
Kang C. Kang C. Drugs. 2021 Jun;81(8):953-956. doi: 10.1007/s40265-021-01520-2. Drugs. 2021. PMID: 33909276 Review.
Fosdenopterin (Nulibry(TM)) is a synthetic cyclic pyranopterin monophosphate that is being developed by Origin Biosciences (a subsidiary of BridgeBio Pharma) for the treatment of molybdenum cofactor deficiency (MoCD) type A. ...This article summarizes the milestones
Fosdenopterin (Nulibry(TM)) is a synthetic cyclic pyranopterin monophosphate that is being developed by Origin Biosciences (a
Regulatory news: Nulibry (fosdenopterin) approved to reduce the risk of mortality in patients with molybdenum cofactor deficiency type A: FDA approval summary.
Farrell S, Karp J, Hager R, Wang Y, Adeniyi O, Wang J, Li L, Ma L, Peretz J, Summan M, Kong N, White M, Pacanowski M, Price D, Filie J, Donohue K, Joffe H. Farrell S, et al. J Inherit Metab Dis. 2021 Sep;44(5):1085-1087. doi: 10.1002/jimd.12421. Epub 2021 Aug 8. J Inherit Metab Dis. 2021. PMID: 34337775 Review. No abstract available.
Successful treatment of molybdenum cofactor deficiency type A with cPMP.
Veldman A, Santamaria-Araujo JA, Sollazzo S, Pitt J, Gianello R, Yaplito-Lee J, Wong F, Ramsden CA, Reiss J, Cook I, Fairweather J, Schwarz G. Veldman A, et al. Pediatrics. 2010 May;125(5):e1249-54. doi: 10.1542/peds.2009-2192. Epub 2010 Apr 12. Pediatrics. 2010. PMID: 20385644