Selumetinib in Children with Inoperable Plexiform Neurofibromas.
N Engl J Med. 2020 Apr 9;382(15):1430-1442. doi: 10.1056/NEJMoa1912735. Epub 2020 Mar 18.
N Engl J Med. 2020.
PMID: 32187457
Free PMC article.
Clinical Trial.