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Table representation of search results timeline featuring number of search results per year.

Year Number of Results
2009 1
2012 2
2013 2
2014 1
2015 5
2016 5
2017 2
2018 1
2019 2
2020 4
2021 7
2022 4
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29 results
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Page 1
Current Clinical Applications of In Vivo Gene Therapy with AAVs.
Mendell JR, Al-Zaidy SA, Rodino-Klapac LR, Goodspeed K, Gray SJ, Kay CN, Boye SL, Boye SE, George LA, Salabarria S, Corti M, Byrne BJ, Tremblay JP. Mendell JR, et al. Among authors: corti m. Mol Ther. 2021 Feb 3;29(2):464-488. doi: 10.1016/j.ymthe.2020.12.007. Epub 2020 Dec 10. Mol Ther. 2021. PMID: 33309881 Free PMC article. Review.
Safety and Efficacy of Omaveloxolone in Friedreich Ataxia (MOXIe Study).
Lynch DR, Chin MP, Delatycki MB, Subramony SH, Corti M, Hoyle JC, Boesch S, Nachbauer W, Mariotti C, Mathews KD, Giunti P, Wilmot G, Zesiewicz T, Perlman S, Goldsberry A, O'Grady M, Meyer CJ. Lynch DR, et al. Among authors: corti m. Ann Neurol. 2021 Feb;89(2):212-225. doi: 10.1002/ana.25934. Epub 2020 Nov 5. Ann Neurol. 2021. PMID: 33068037 Free PMC article. Clinical Trial.
Considerations for Systemic Use of Gene Therapy.
Byrne BJ, Corti M, Muntoni F. Byrne BJ, et al. Among authors: corti m. Mol Ther. 2021 Feb 3;29(2):422-423. doi: 10.1016/j.ymthe.2021.01.016. Epub 2021 Jan 14. Mol Ther. 2021. PMID: 33485465 Free PMC article. Review. No abstract available.
Scratching the surface of RGD-directed AAV capsid engineering.
Zolotukhin S, Trivedi PD, Corti M, Byrne BJ. Zolotukhin S, et al. Among authors: corti m. Mol Ther. 2021 Nov 3;29(11):3099-3100. doi: 10.1016/j.ymthe.2021.10.020. Epub 2021 Oct 26. Mol Ther. 2021. PMID: 34699781 Free PMC article. No abstract available.
Adeno-associated virus-mediated gene therapy for metabolic myopathy.
Mah CS, Soustek MS, Todd AG, McCall A, Smith BK, Corti M, Falk DJ, Byrne BJ. Mah CS, et al. Among authors: corti m. Hum Gene Ther. 2013 Nov;24(11):928-36. doi: 10.1089/hum.2013.2514. Hum Gene Ther. 2013. PMID: 24164240 Free PMC article. Review.
The respiratory neuromuscular system in Pompe disease.
Fuller DD, ElMallah MK, Smith BK, Corti M, Lawson LA, Falk DJ, Byrne BJ. Fuller DD, et al. Among authors: corti m. Respir Physiol Neurobiol. 2013 Nov 1;189(2):241-9. doi: 10.1016/j.resp.2013.06.007. Epub 2013 Jun 21. Respir Physiol Neurobiol. 2013. PMID: 23797185 Free PMC article. Review.
Targeted approaches to induce immune tolerance for Pompe disease therapy.
Doerfler PA, Nayak S, Corti M, Morel L, Herzog RW, Byrne BJ. Doerfler PA, et al. Among authors: corti m. Mol Ther Methods Clin Dev. 2016 Jan 27;3:15053. doi: 10.1038/mtm.2015.53. eCollection 2016. Mol Ther Methods Clin Dev. 2016. PMID: 26858964 Free PMC article. Review.
Reply: Respiratory motor function in centronuclear myopathy.
Smith BK, Renno MS, Martin AD, Corti M, Byrne BJ. Smith BK, et al. Among authors: corti m. Muscle Nerve. 2016 Apr;53(4):660-1. doi: 10.1002/mus.24961. Epub 2015 Dec 29. Muscle Nerve. 2016. PMID: 26561983 No abstract available.
29 results