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Strengthening health systems for access to gene therapy in rare genetic disorders.
Bhatia S, Le Cam Y, Carrion J, Diamond L, Fennessy P, Gassman S, Gutzwiller F, Kagan S, Pankevich D, Young Maloney J, Mahadev N, Schulz M, Wong-Rieger D, Morgese P. Bhatia S, et al. Among authors: morgese p. Mol Ther Methods Clin Dev. 2024 Mar 13;32(2):101220. doi: 10.1016/j.omtm.2024.101220. eCollection 2024 Jun 13. Mol Ther Methods Clin Dev. 2024. PMID: 38516694 Free PMC article. No abstract available.