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Table representation of search results timeline featuring number of search results per year.

Year Number of Results
2006 1
2008 3
2009 4
2010 2
2011 6
2012 3
2013 2
2014 4
2015 7
2016 3
2017 2
2021 1
2022 1
2023 1
2024 0

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37 results

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Page 1
Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy.
Mendell JR, Al-Zaidy S, Shell R, Arnold WD, Rodino-Klapac LR, Prior TW, Lowes L, Alfano L, Berry K, Church K, Kissel JT, Nagendran S, L'Italien J, Sproule DM, Wells C, Cardenas JA, Heitzer MD, Kaspar A, Corcoran S, Braun L, Likhite S, Miranda C, Meyer K, Foust KD, Burghes AHM, Kaspar BK. Mendell JR, et al. Among authors: foust kd. N Engl J Med. 2017 Nov 2;377(18):1713-1722. doi: 10.1056/NEJMoa1706198. N Engl J Med. 2017. PMID: 29091557 Free article. Clinical Trial.
Biodistribution of onasemnogene abeparvovec DNA, mRNA and SMN protein in human tissue.
Thomsen G, Burghes AHM, Hsieh C, Do J, Chu BTT, Perry S, Barkho B, Kaufmann P, Sproule DM, Feltner DE, Chung WK, McGovern VL, Hevner RF, Conces M, Pierson CR, Scoto M, Muntoni F, Mendell JR, Foust KD. Thomsen G, et al. Among authors: foust kd. Nat Med. 2021 Oct;27(10):1701-1711. doi: 10.1038/s41591-021-01483-7. Epub 2021 Oct 4. Nat Med. 2021. PMID: 34608334 Clinical Trial.
Novel MECP2 gene therapy is effective in a multicenter study using two mouse models of Rett syndrome and is safe in non-human primates.
Powers S, Likhite S, Gadalla KK, Miranda CJ, Huffenberger AJ, Dennys C, Foust KD, Morales P, Pierson CR, Rinaldi F, Perry S, Bolon B, Wein N, Cobb S, Kaspar BK, Meyer KC. Powers S, et al. Among authors: foust kd. Mol Ther. 2023 Sep 6;31(9):2767-2782. doi: 10.1016/j.ymthe.2023.07.013. Epub 2023 Jul 22. Mol Ther. 2023. PMID: 37481701 Free article.
Intravenous injections in neonatal mice.
Gombash Lampe SE, Kaspar BK, Foust KD. Gombash Lampe SE, et al. Among authors: foust kd. J Vis Exp. 2014 Nov 11;(93):e52037. doi: 10.3791/52037. J Vis Exp. 2014. PMID: 25407048 Free PMC article.
Systemic Gene Therapy for Targeting the CNS.
Gombash SE, Foust KD. Gombash SE, et al. Among authors: foust kd. Methods Mol Biol. 2016;1382:231-7. doi: 10.1007/978-1-4939-3271-9_16. Methods Mol Biol. 2016. PMID: 26611590
A role for glia in the progression of Rett's syndrome.
Lioy DT, Garg SK, Monaghan CE, Raber J, Foust KD, Kaspar BK, Hirrlinger PG, Kirchhoff F, Bissonnette JM, Ballas N, Mandel G. Lioy DT, et al. Among authors: foust kd. Nature. 2011 Jun 29;475(7357):497-500. doi: 10.1038/nature10214. Nature. 2011. PMID: 21716289 Free PMC article.
37 results