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Table representation of search results timeline featuring number of search results per year.

Year Number of Results
1994 2
1995 1
1997 2
1998 2
1999 1
2000 8
2001 6
2002 3
2003 3
2004 9
2005 9
2006 7
2007 12
2008 6
2009 12
2010 7
2011 14
2012 9
2013 10
2014 15
2015 13
2016 9
2017 13
2018 9
2019 5
2020 5
2021 8
2022 6
2023 3
2024 1

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186 results

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Page 1
Lentiviral gene therapy for X-linked chronic granulomatous disease.
Kohn DB, Booth C, Kang EM, Pai SY, Shaw KL, Santilli G, Armant M, Buckland KF, Choi U, De Ravin SS, Dorsey MJ, Kuo CY, Leon-Rico D, Rivat C, Izotova N, Gilmour K, Snell K, Dip JX, Darwish J, Morris EC, Terrazas D, Wang LD, Bauser CA, Paprotka T, Kuhns DB, Gregg J, Raymond HE, Everett JK, Honnet G, Biasco L, Newburger PE, Bushman FD, Grez M, Gaspar HB, Williams DA, Malech HL, Galy A, Thrasher AJ; Net4CGD consortium. Kohn DB, et al. Among authors: gaspar hb. Nat Med. 2020 Feb;26(2):200-206. doi: 10.1038/s41591-019-0735-5. Epub 2020 Jan 27. Nat Med. 2020. PMID: 31988463 Free PMC article. Clinical Trial.
Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy.
Eichler F, Duncan C, Musolino PL, Orchard PJ, De Oliveira S, Thrasher AJ, Armant M, Dansereau C, Lund TC, Miller WP, Raymond GV, Sankar R, Shah AJ, Sevin C, Gaspar HB, Gissen P, Amartino H, Bratkovic D, Smith NJC, Paker AM, Shamir E, O'Meara T, Davidson D, Aubourg P, Williams DA. Eichler F, et al. Among authors: gaspar hb. N Engl J Med. 2017 Oct 26;377(17):1630-1638. doi: 10.1056/NEJMoa1700554. Epub 2017 Oct 4. N Engl J Med. 2017. PMID: 28976817 Free PMC article. Clinical Trial.
Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency.
Kohn DB, Booth C, Shaw KL, Xu-Bayford J, Garabedian E, Trevisan V, Carbonaro-Sarracino DA, Soni K, Terrazas D, Snell K, Ikeda A, Leon-Rico D, Moore TB, Buckland KF, Shah AJ, Gilmour KC, De Oliveira S, Rivat C, Crooks GM, Izotova N, Tse J, Adams S, Shupien S, Ricketts H, Davila A, Uzowuru C, Icreverzi A, Barman P, Campo Fernandez B, Hollis RP, Coronel M, Yu A, Chun KM, Casas CE, Zhang R, Arduini S, Lynn F, Kudari M, Spezzi A, Zahn M, Heimke R, Labik I, Parrott R, Buckley RH, Reeves L, Cornetta K, Sokolic R, Hershfield M, Schmidt M, Candotti F, Malech HL, Thrasher AJ, Gaspar HB. Kohn DB, et al. Among authors: gaspar hb. N Engl J Med. 2021 May 27;384(21):2002-2013. doi: 10.1056/NEJMoa2027675. Epub 2021 May 11. N Engl J Med. 2021. PMID: 33974366 Free PMC article. Clinical Trial.
Relevance of biallelic versus monoallelic TNFRSF13B mutations in distinguishing disease-causing from risk-increasing TNFRSF13B variants in antibody deficiency syndromes.
Salzer U, Bacchelli C, Buckridge S, Pan-Hammarström Q, Jennings S, Lougaris V, Bergbreiter A, Hagena T, Birmelin J, Plebani A, Webster AD, Peter HH, Suez D, Chapel H, McLean-Tooke A, Spickett GP, Anover-Sombke S, Ochs HD, Urschel S, Belohradsky BH, Ugrinovic S, Kumararatne DS, Lawrence TC, Holm AM, Franco JL, Schulze I, Schneider P, Gertz EM, Schäffer AA, Hammarström L, Thrasher AJ, Gaspar HB, Grimbacher B. Salzer U, et al. Among authors: gaspar hb. Blood. 2009 Feb 26;113(9):1967-76. doi: 10.1182/blood-2008-02-141937. Epub 2008 Nov 3. Blood. 2009. PMID: 18981294 Free PMC article.
Gene Therapy Approaches to Immunodeficiency.
Ghosh S, Gaspar HB. Ghosh S, et al. Among authors: gaspar hb. Hematol Oncol Clin North Am. 2017 Oct;31(5):823-834. doi: 10.1016/j.hoc.2017.05.003. Epub 2017 Jun 29. Hematol Oncol Clin North Am. 2017. PMID: 28895850 Free article. Review.
Treating Immunodeficiency through HSC Gene Therapy.
Booth C, Gaspar HB, Thrasher AJ. Booth C, et al. Among authors: gaspar hb. Trends Mol Med. 2016 Apr;22(4):317-327. doi: 10.1016/j.molmed.2016.02.002. Epub 2016 Mar 15. Trends Mol Med. 2016. PMID: 26993219 Free article. Review.
Gene therapy for haemophagocytic lymphohistiocytosis.
Booth C, Carmo M, Gaspar HB. Booth C, et al. Among authors: gaspar hb. Curr Gene Ther. 2014;14(6):437-46. doi: 10.2174/1566523214666140918112113. Curr Gene Ther. 2014. PMID: 25245087 Review.
Early B cell defects.
Gaspar HB, Conley ME. Gaspar HB, et al. Clin Exp Immunol. 2000 Mar;119(3):383-9. doi: 10.1046/j.1365-2249.2000.01192.x. Clin Exp Immunol. 2000. PMID: 10691907 Free PMC article. Review. No abstract available.
Gene therapy for primary immunodeficiency.
Booth C, Gaspar HB, Thrasher AJ. Booth C, et al. Among authors: gaspar hb. Curr Opin Pediatr. 2011 Dec;23(6):659-66. doi: 10.1097/MOP.0b013e32834cd67a. Curr Opin Pediatr. 2011. PMID: 21970832 Review.
186 results