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Table representation of search results timeline featuring number of search results per year.

Year Number of Results
1954 2
1956 1
1957 5
1958 1
1959 1
1960 1
1961 2
1962 3
1963 1
1968 1
1969 2
1970 1
1971 1
1973 1
1974 1
1976 2
1977 3
1978 7
1979 4
1980 4
1981 7
1982 10
1983 6
1984 16
1985 14
1986 14
1987 12
1988 16
1989 28
1990 22
1991 14
1992 14
1993 20
1994 21
1995 17
1996 15
1997 15
1998 17
1999 12
2000 7
2001 11
2002 12
2003 12
2004 18
2005 16
2006 12
2007 27
2008 20
2009 17
2010 17
2011 20
2012 28
2013 30
2014 29
2015 47
2016 36
2017 44
2018 42
2019 43
2020 51
2021 50
2022 57
2023 46
2024 52
2025 35

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1,023 results

Results by year

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Page 1
Patient-Specific In Vivo Gene Editing to Treat a Rare Genetic Disease.
Musunuru K, Grandinette SA, Wang X, Hudson TR, Briseno K, Berry AM, Hacker JL, Hsu A, Silverstein RA, Hille LT, Ogul AN, Robinson-Garvin NA, Small JC, McCague S, Burke SM, Wright CM, Bick S, Indurthi V, Sharma S, Jepperson M, Vakulskas CA, Collingwood M, Keogh K, Jacobi A, Sturgeon M, Brommel C, Schmaljohn E, Kurgan G, Osborne T, Zhang H, Kinney K, Rettig G, Barbosa CJ, Semple SC, Tam YK, Lutz C, George LA, Kleinstiver BP, Liu DR, Ng K, Kassim SH, Giannikopoulos P, Alameh MG, Urnov FD, Ahrens-Nicklas RC. Musunuru K, et al. Among authors: george la. N Engl J Med. 2025 Jun 12;392(22):2235-2243. doi: 10.1056/NEJMoa2504747. Epub 2025 May 15. N Engl J Med. 2025. PMID: 40373211
Roctavian gene therapy for hemophilia A.
Samelson-Jones BJ, Small JC, George LA. Samelson-Jones BJ, et al. Among authors: george la. Blood Adv. 2024 Oct 8;8(19):5179-5189. doi: 10.1182/bloodadvances.2023011847. Blood Adv. 2024. PMID: 38991118 Free PMC article. Review.
Blinatumomab for First-Line Treatment of Children and Young Persons With B-ALL.
Hodder A, Mishra AK, Enshaei A, Baird S, Elbeshlawi I, Bonney D, Clesham K, Cummins M, Vedi A, Gibson B, George L, Ingham D, Jigoulina G, Lancaster D, Lindsay K, Madni M, Malone A, Mitchell B, Moppett J, Motwani J, Moorman AV, Patrick K, Samrin L, Tewari S, Thakur I, O'Connor D, Samarasinghe S, Vora A. Hodder A, et al. Among authors: george l. J Clin Oncol. 2024 Mar 10;42(8):907-914. doi: 10.1200/JCO.23.01392. Epub 2023 Nov 15. J Clin Oncol. 2024. PMID: 37967307
Intra-condensate demixing of TDP-43 inside stress granules generates pathological aggregates.
Yan X, Kuster D, Mohanty P, Nijssen J, Pombo-García K, Rizuan A, Franzmann TM, Sergeeva A, Passos PM, George L, Wang SH, Shenoy J, Danielson HL, Honigmann A, Ayala YM, Fawzi NL, Mittal J, Alberti S, Hyman AA. Yan X, et al. Among authors: george l. bioRxiv [Preprint]. 2024 May 24:2024.01.23.576837. doi: 10.1101/2024.01.23.576837. bioRxiv. 2024. Update in: Cell. 2025 May 15:S0092-8674(25)00509-4. doi: 10.1016/j.cell.2025.04.039. PMID: 38328053 Free PMC article. Updated. Preprint.
Multiyear Factor VIII Expression after AAV Gene Transfer for Hemophilia A.
George LA, Monahan PE, Eyster ME, Sullivan SK, Ragni MV, Croteau SE, Rasko JEJ, Recht M, Samelson-Jones BJ, MacDougall A, Jaworski K, Noble R, Curran M, Kuranda K, Mingozzi F, Chang T, Reape KZ, Anguela XM, High KA. George LA, et al. N Engl J Med. 2021 Nov 18;385(21):1961-1973. doi: 10.1056/NEJMoa2104205. N Engl J Med. 2021. PMID: 34788507 Free PMC article. Clinical Trial.
Intra-condensate demixing of TDP-43 inside stress granules generates pathological aggregates.
Yan X, Kuster D, Mohanty P, Nijssen J, Pombo-García K, Garcia Morato J, Rizuan A, Franzmann TM, Sergeeva A, Ly AM, Liu F, Passos PM, George L, Wang SH, Shenoy J, Danielson HL, Ozguney B, Honigmann A, Ayala YM, Fawzi NL, Dickson DW, Rossoll W, Mittal J, Alberti S, Hyman AA. Yan X, et al. Among authors: george l. Cell. 2025 May 15:S0092-8674(25)00509-4. doi: 10.1016/j.cell.2025.04.039. Online ahead of print. Cell. 2025. PMID: 40412392 Free article.
Current clinical applications of AAV-mediated gene therapy.
Byrne BJ, Flanigan KM, Matesanz SE, Finkel RS, Waldrop MA, D'Ambrosio ES, Johnson NE, Smith BK, Bönnemann C, Carrig S, Rossano JW, Greenberg B, Lalaguna L, Lara-Pezzi E, Subramony S, Corti M, Mercado-Rodriguez C, Leon-Astudillo C, Ahrens-Nicklas R, Bharucha-Goebel D, Gao G, Gessler DJ, Hwu WL, Chien YH, Lee NC, Boye SL, Boye SE, George LA. Byrne BJ, et al. Among authors: george la. Mol Ther. 2025 Jun 4;33(6):2479-2516. doi: 10.1016/j.ymthe.2025.04.045. Epub 2025 May 5. Mol Ther. 2025. PMID: 40329530 Free article. Review.
Coagulation factor VIII regulates von Willebrand factor homeostasis invivo.
Cao W, Trask AR, Bignotti AI, George LA, Doshi BS, Sabatino DE, Yada N, Zheng L, Camire RM, Zheng XL. Cao W, et al. Among authors: george la. J Thromb Haemost. 2023 Dec;21(12):3477-3489. doi: 10.1016/j.jtha.2023.09.004. Epub 2023 Sep 17. J Thromb Haemost. 2023. PMID: 37726033 Free PMC article.
Elongator regulates the melanocortin satiety pathway.
Walters J, Walters C, Cameron B, George L. Walters J, et al. Among authors: george l. Biochem Biophys Res Commun. 2022 Jul 12;613:73-80. doi: 10.1016/j.bbrc.2022.04.128. Epub 2022 May 2. Biochem Biophys Res Commun. 2022. PMID: 35537288 Free PMC article.
1,023 results