Adenovirus-associated virus vector-mediated gene transfer in hemophilia B.
N Engl J Med. 2011 Dec 22;365(25):2357-65. doi: 10.1056/NEJMoa1108046. Epub 2011 Dec 10.
N Engl J Med. 2011.
PMID: 22149959
Free PMC article.
Clinical Trial.