Natural history of Type 2 and 3 spinal muscular atrophy: 2-year NatHis-SMA study.
Ann Clin Transl Neurol. 2021 Feb;8(2):359-373. doi: 10.1002/acn3.51281. Epub 2020 Dec 24.
Ann Clin Transl Neurol. 2021.
PMID: 33369268
Free PMC article.