Loss of the sphingolipid desaturase DEGS1 causes hypomyelinating leukodystrophy.
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J Clin Invest. 2019 Mar 1;129(3):1240-1256. doi: 10.1172/JCI123959. Epub 2019 Feb 11.
J Clin Invest. 2019.
PMID: 30620337
Free PMC article.