Open reading frame correction using splice-switching antisense oligonucleotides for the treatment of cystic fibrosis.
Proc Natl Acad Sci U S A. 2022 Jan 18;119(3):e2114886119. doi: 10.1073/pnas.2114886119.
Proc Natl Acad Sci U S A. 2022.
PMID: 35017302
Free PMC article.