Combination therapies in spinal muscular atrophy: a systematic review.
Bemanalizadeh M, Heidary L, Dakkali MS, Hadizadeh S, Ahmadbeigi N, Heidari M, Zamani G, Ashrafi M, Mansouri V.
Bemanalizadeh M, et al.
Eur J Pediatr. 2025 Aug 29;184(9):583. doi: 10.1007/s00431-025-06386-0.
Eur J Pediatr. 2025.
PMID: 40879810
A total of 29 individual patients receiving combination therapies (dual: n = 26, triple: n = 3) were analyzed. Switching therapies were the most common, particularly from nusinersen or risdiplam to onasemnogene abeparvovec-xioi. ...
A total of 29 individual patients receiving combination therapies (dual: n = 26, triple: n = 3) were analyzed. Switching thera …