Assessing the value of orphan drugs using conventional cost-effectiveness analysis: Is it fit for purpose?
Orphanet J Rare Dis. 2022 Apr 5;17(1):157. doi: 10.1186/s13023-022-02283-z.
Orphanet J Rare Dis. 2022.
PMID: 35382853
Free PMC article.
Review.