The nucleotide prodrug CERC-913 improves mtDNA content in primary hepatocytes from DGUOK-deficient rats.
J Inherit Metab Dis. 2021 Mar;44(2):492-501. doi: 10.1002/jimd.12354. Epub 2021 Jan 15.
J Inherit Metab Dis. 2021.
PMID: 33368311