European ad-hoc consensus statement on gene replacement therapy for spinal muscular atrophy.
Eur J Paediatr Neurol. 2020 Sep;28:38-43. doi: 10.1016/j.ejpn.2020.07.001. Epub 2020 Jul 9.
Eur J Paediatr Neurol. 2020.
PMID: 32763124
Free PMC article.