In vivo adenine base editing of PCSK9 in macaques reduces LDL cholesterol levels.
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Rothgangl T, et al. Among authors: villiger l.
Nat Biotechnol. 2021 Aug;39(8):949-957. doi: 10.1038/s41587-021-00933-4. Epub 2021 May 19.
Nat Biotechnol. 2021.
PMID: 34012094
Free PMC article.