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Table representation of search results timeline featuring number of search results per year.

Year Number of Results
2013 1
2014 5
2015 10
2016 13
2017 8
2018 7
2019 7
2020 6
2021 8
2022 3
2023 5
2024 2
2025 4
2026 0

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Cited In for PMID: 23863630

71 results

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Page 1
β-globin gene transfer to human bone marrow for sickle cell disease.
Romero Z, Urbinati F, Geiger S, Cooper AR, Wherley J, Kaufman ML, Hollis RP, de Assin RR, Senadheera S, Sahagian A, Jin X, Gellis A, Wang X, Gjertson D, Deoliveira S, Kempert P, Shupien S, Abdel-Azim H, Walters MC, Meiselman HJ, Wenby RB, Gruber T, Marder V, Coates TD, Kohn DB. Romero Z, et al. J Clin Invest. 2013 Jul 1;123(8):3317-30. doi: 10.1172/JCI67930. Online ahead of print. J Clin Invest. 2013. PMID: 23863630 Free PMC article.
Lentiviral vectors for hematopoietic stem cell gene therapy restore α-globin expression in α-thalassemia red blood cells.
Segura EER, Hart K, Campo Fernandez B, Brown D, Tam K, Gutierrez Garcia A, Seigneurbieux E, Li K, Mulumba C, Blakely E, Masiuk K, Sinha R, Sharma D, Everett J, Hogenauer M, Cromer MK, Bushman F, MacKenzie TC, Kohn DB. Segura EER, et al. Cell Rep Med. 2025 Oct 21;6(10):102362. doi: 10.1016/j.xcrm.2025.102362. Epub 2025 Sep 17. Cell Rep Med. 2025. PMID: 40967220 Free PMC article.
Preclinical quality, safety, and efficacy of a CGMP iPSC-derived myogenic progenitor product for the treatment of muscular dystrophies.
Azzag K, Magli A, Kiley J, Sumstad D, Kadidlo D, Crist SB, Norris B, Ahlquist A, Hocum Stone LL, Everett J, Shappa Faustich J, Seelig D, Rangarajan P, Kim H, Flory C, Bushman F, Ramachandran S, Kang PB, Schumacher RJ, Wagner JE, Kyba M, Graham ML, McKenna DH, Perlingeiro RCR. Azzag K, et al. Mol Ther. 2025 Oct 1;33(10):5099-5117. doi: 10.1016/j.ymthe.2025.07.007. Epub 2025 Jul 17. Mol Ther. 2025. PMID: 40682272 Free PMC article.
Lentiviral gene therapy with reduced-intensity conditioning for sickle cell disease: a phase 1/2 trial.
Grimley M, Davies SM, Shrestha A, Shova A, Asnani M, Kent M, Sayani F, Quinn CT, Niss O, Lutzko C, Mehta PA, Khandelwal P, Little C, Chandra S, Felker S, Chi M, Kalfa TA, Knight-Madden J, Arumugam PI, Ramos KN, Witting S, Latham T, Bushman FD, Malik P. Grimley M, et al. Nat Med. 2025 Jul;31(7):2204-2212. doi: 10.1038/s41591-025-03662-2. Epub 2025 May 26. Nat Med. 2025. PMID: 40419809 Free PMC article. Clinical Trial.
71 results