Efficacy and safety of N-acetyl-L-leucine in patients with ataxia telangiectasia: A randomized, double-blind, placebo-controlled, crossover clinical trial.
Eur J Paediatr Neurol. 2024 May;50:57-63. doi: 10.1016/j.ejpn.2024.04.009. Epub 2024 Apr 22.
Eur J Paediatr Neurol. 2024.
PMID: 38669738
Clinical Trial.