Cystic fibrosis.
Lancet. 2016 Nov 19;388(10059):2519-2531. doi: 10.1016/S0140-6736(16)00576-6. Epub 2016 Apr 29.
Lancet. 2016.
PMID: 27140670
Review.
Cystic fibrosis is a common life-limiting autosomal recessive genetic disorder, with highest prevalence in Europe, North America, and Australia. ...Further small molecule and gene-based therapies are being developed to restore CFTR function; these therapies promise …
Cystic fibrosis is a common life-limiting autosomal recessive genetic disorder, with highest prevalence in Europe, North Ameri …