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2021 2
2022 34
2023 1
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34 results
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Page 1
Neoantigen T-Cell Receptor Gene Therapy in Pancreatic Cancer.
Leidner R, Sanjuan Silva N, Huang H, Sprott D, Zheng C, Shih YP, Leung A, Payne R, Sutcliffe K, Cramer J, Rosenberg SA, Fox BA, Urba WJ, Tran E. Leidner R, et al. N Engl J Med. 2022 Jun 2;386(22):2112-2119. doi: 10.1056/NEJMoa2119662. N Engl J Med. 2022. PMID: 35648703 Free PMC article.
Immunogenicity and toxicity of AAV gene therapy.
Ertl HCJ. Ertl HCJ. Front Immunol. 2022 Aug 12;13:975803. doi: 10.3389/fimmu.2022.975803. eCollection 2022. Front Immunol. 2022. PMID: 36032092 Free PMC article. Review.
Phase 1-2 Trial of AAVS3 Gene Therapy in Patients with Hemophilia B.
Chowdary P, Shapiro S, Makris M, Evans G, Boyce S, Talks K, Dolan G, Reiss U, Phillips M, Riddell A, Peralta MR, Quaye M, Patch DW, Tuddenham E, Dane A, Watissée M, Long A, Nathwani A. Chowdary P, et al. N Engl J Med. 2022 Jul 21;387(3):237-247. doi: 10.1056/NEJMoa2119913. N Engl J Med. 2022. PMID: 35857660 Free article. Clinical Trial.
AAV vectors: The Rubik's cube of human gene therapy.
Pupo A, Fernández A, Low SH, François A, Suárez-Amarán L, Samulski RJ. Pupo A, et al. Mol Ther. 2022 Dec 7;30(12):3515-3541. doi: 10.1016/j.ymthe.2022.09.015. Epub 2022 Oct 5. Mol Ther. 2022. PMID: 36203359 Free article. Review.
On-demand cell-autonomous gene therapy for brain circuit disorders.
Qiu Y, O'Neill N, Maffei B, Zourray C, Almacellas-Barbanoj A, Carpenter JC, Jones SP, Leite M, Turner TJ, Moreira FC, Snowball A, Shekh-Ahmad T, Magloire V, Barral S, Kurian MA, Walker MC, Schorge S, Kullmann DM, Lignani G. Qiu Y, et al. Science. 2022 Nov 4;378(6619):523-532. doi: 10.1126/science.abq6656. Epub 2022 Nov 3. Science. 2022. PMID: 36378958 Free PMC article.
Three-Year Safety Results of SAR422459 (EIAV-ABCA4) Gene Therapy in Patients With ABCA4-Associated Stargardt Disease: An Open-Label Dose-Escalation Phase I/IIa Clinical Trial, Cohorts 1-5.
Parker MA, Erker LR, Audo I, Choi D, Mohand-Said S, Sestakauskas K, Benoit P, Appelqvist T, Krahmer M, Ségaut-Prévost C, Lujan BJ, Faridi A, Chegarnov EN, Steinkamp PN, Ku C, da Palma MM, Barale PO, Ayelo-Scheer S, Lauer A, Stout T, Wilson DJ, Weleber RG, Pennesi ME, Sahel JA, Yang P. Parker MA, et al. Am J Ophthalmol. 2022 Aug;240:285-301. doi: 10.1016/j.ajo.2022.02.013. Epub 2022 Mar 4. Am J Ophthalmol. 2022. PMID: 35248547 Free PMC article. Clinical Trial.
Gene therapy clinical trials, where do we go? An overview.
Arabi F, Mansouri V, Ahmadbeigi N. Arabi F, et al. Biomed Pharmacother. 2022 Sep;153:113324. doi: 10.1016/j.biopha.2022.113324. Epub 2022 Jun 29. Biomed Pharmacother. 2022. PMID: 35779421 Free article. Review.
Cryo-electron Microscopy of Adeno-associated Virus.
Stagg SM, Yoshioka C, Davulcu O, Chapman MS. Stagg SM, et al. Chem Rev. 2022 Sep 14;122(17):14018-14054. doi: 10.1021/acs.chemrev.1c00936. Epub 2022 May 16. Chem Rev. 2022. PMID: 35575684 Free PMC article. Review.
34 results