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2020 2
2021 8
2022 5
2024 0

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14 results

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Page 1
Novel AAV capsids for intravitreal gene therapy of photoreceptor disorders.
Pavlou M, Schön C, Occelli LM, Rossi A, Meumann N, Boyd RF, Bartoe JT, Siedlecki J, Gerhardt MJ, Babutzka S, Bogedein J, Wagner JE, Priglinger SG, Biel M, Petersen-Jones SM, Büning H, Michalakis S. Pavlou M, et al. EMBO Mol Med. 2021 Apr 9;13(4):e13392. doi: 10.15252/emmm.202013392. Epub 2021 Feb 22. EMBO Mol Med. 2021. PMID: 33616280 Free PMC article.
Current Clinical Applications of In Vivo Gene Therapy with AAVs.
Mendell JR, Al-Zaidy SA, Rodino-Klapac LR, Goodspeed K, Gray SJ, Kay CN, Boye SL, Boye SE, George LA, Salabarria S, Corti M, Byrne BJ, Tremblay JP. Mendell JR, et al. Mol Ther. 2021 Feb 3;29(2):464-488. doi: 10.1016/j.ymthe.2020.12.007. Epub 2020 Dec 10. Mol Ther. 2021. PMID: 33309881 Free PMC article. Review.
The new landscape of retinal gene therapy.
Ku CA, Pennesi ME. Ku CA, et al. Am J Med Genet C Semin Med Genet. 2020 Sep;184(3):846-859. doi: 10.1002/ajmg.c.31842. Epub 2020 Sep 5. Am J Med Genet C Semin Med Genet. 2020. PMID: 32888388 Review.
Viral Vector Technologies and Strategies: Improving on Nature.
Croze RH, Kotterman M, Burns CH, Schmitt CE, Quezada M, Schaffer D, Kirn D, Francis P. Croze RH, et al. Int Ophthalmol Clin. 2021 Jul 1;61(3):59-89. doi: 10.1097/IIO.0000000000000361. Int Ophthalmol Clin. 2021. PMID: 34196318 Free PMC article. No abstract available.
Gene Therapy for Rhodopsin Mutations.
Lewin AS, Smith WC. Lewin AS, et al. Cold Spring Harb Perspect Med. 2022 Aug 8;12(9):a041283. doi: 10.1101/cshperspect.a041283. Online ahead of print. Cold Spring Harb Perspect Med. 2022. PMID: 35940643
14 results