Antisense oligonucleotides extend survival and reverse decrement in muscle response in ALS models.
J Clin Invest. 2018 Aug 1;128(8):3558-3567. doi: 10.1172/JCI99081. Epub 2018 Jul 16.
J Clin Invest. 2018.
PMID: 30010620
Free PMC article.