Long-term treatment of hereditary transthyretin amyloidosis with patisiran: multicentre, real-world experience in Italy.
Gentile L, Mazzeo A, Briani C, Casagrande S, De Luca M, Fabrizi GM, Gagliardi C, Gemelli C, Forcina F, Grandis M, Guglielmino V, Iabichella G, Leonardi L, Lozza A, Manganelli F, Mussinelli R, My F, Occhipinti G, Fenu S, Russo M, Romano A, Salvalaggio A, Tagliapietra M, Tozza S, Palladini G, Obici L, Luigetti M.
Gentile L, et al.
Neurol Sci. 2024 Apr 16. doi: 10.1007/s10072-024-07494-9. Online ahead of print.
Neurol Sci. 2024.
PMID: 38622453
In this population, the mean NIS at baseline was 71.4 ( 27.8); mBMI, 917.1 ( 207) kg/m(2); KPS, 67.1 ( 14.0); Norfolk QoL-DN, 62.2 ( 25.2); and CADT, 13.2 ( 3.3). ...
In this population, the mean NIS at baseline was 71.4 ( 27.8); mBMI, 917.1 ( 207) kg/m(2); KPS, 67.1 ( 14.0); Norfolk QoL-DN, 62.2 ( …