Base editing HbS to HbG-Makassar improves hemoglobin function supporting its use in sickle cell disease.
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Nat Commun. 2025 Feb 7;16(1):1441. doi: 10.1038/s41467-025-56578-3.
Nat Commun. 2025.
PMID: 39920120
Free PMC article.