First-in-human clinical study of an embryonic stem cell product for urea cycle disorders.
Umezawa A, Fukuda A, Horikawa R, Uchida H, Enosawa S, Oishi Y, Nakamura N, Sasaki K, Yanagi Y, Shimizu S, Nakao T, Kodama T, Sakamoto S, Hayakawa I, Akiyama S, Saku N, Miyata S, Ite K, Javaregowda PK, Toyoda M, Nonaka H, Nakamura K, Ito Y, Fukuhara Y, Miyazaki O, Nosaka S, Nakabayashi K, Haga C, Yoshioka T, Masuda A, Ohkura T, Yamazaki-Inoue M, Machida M, Abutani-Sakamoto R, Miyajima S, Akutsu H, Matsubara Y, Igarashi T, Kasahara M.
Umezawa A, et al. Among authors: uchida h.
Stem Cell Res Ther. 2025 Mar 6;16(1):120. doi: 10.1186/s13287-025-04162-3.
Stem Cell Res Ther. 2025.
PMID: 40050977
Free PMC article.