In Utero Hematopoietic Cell Transplantation in Fetuses with Alpha Thalassemia Major: A Phase 1 Clinical Trial.
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MacKenzie TC, et al. Among authors: kharbanda s.
Blood Adv. 2026 Apr 15:bloodadvances.2026019655. doi: 10.1182/bloodadvances.2026019655. Online ahead of print.
Blood Adv. 2026.
PMID: 41984996