Nanoparticle delivery of CRISPR into the brain rescues a mouse model of fragile X syndrome from exaggerated repetitive behaviours.
Nat Biomed Eng. 2018 Jul;2(7):497-507. doi: 10.1038/s41551-018-0252-8. Epub 2018 Jun 25.
Nat Biomed Eng. 2018.
PMID: 30948824
Free PMC article.