Triple Therapy for Cystic Fibrosis Phe508del-Gating and -Residual Function Genotypes.
N Engl J Med. 2021 Aug 26;385(9):815-825. doi: 10.1056/NEJMoa2100665.
N Engl J Med. 2021.
PMID: 34437784
Free PMC article.
Clinical Trial.