JAK inhibition in a patient with a STAT1 gain-of-function variant reveals STAT1 dysregulation as a common feature of aplastic anemia.
Med (N Y). 2022 Jan 14;3(1):42-57.e5. doi: 10.1016/j.medj.2021.12.003.
Med (N Y). 2022.
PMID: 35590143