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Table representation of search results timeline featuring number of search results per year.
Year | Number of Results |
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2005 | 1 |
2006 | 1 |
2009 | 1 |
2011 | 1 |
2024 | 0 |
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Complete correction of hyperphenylalaninemia following liver-directed, recombinant AAV2/8 vector-mediated gene therapy in murine phenylketonuria.
Gene Ther. 2006 Mar;13(5):457-62. doi: 10.1038/sj.gt.3302678.
Gene Ther. 2006.
PMID: 16319949
Free PMC article.
Low therapeutic threshold for hepatocyte replacement in murine phenylketonuria.
Hamman K, Clark H, Montini E, Al-Dhalimy M, Grompe M, Finegold M, Harding CO.
Hamman K, et al.
Mol Ther. 2005 Aug;12(2):337-44. doi: 10.1016/j.ymthe.2005.03.025.
Mol Ther. 2005.
PMID: 16043102
Free PMC article.
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A Delphi clinical practice protocol for the management of very long chain acyl-CoA dehydrogenase deficiency.
Arnold GL, Van Hove J, Freedenberg D, Strauss A, Longo N, Burton B, Garganta C, Ficicioglu C, Cederbaum S, Harding C, Boles RG, Matern D, Chakraborty P, Feigenbaum A.
Arnold GL, et al.
Mol Genet Metab. 2009 Mar;96(3):85-90. doi: 10.1016/j.ymgme.2008.09.008. Epub 2009 Jan 20.
Mol Genet Metab. 2009.
PMID: 19157942
Free PMC article.
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Hepatocytes from wild-type or heterozygous donors are equally effective in achieving successful therapeutic liver repopulation in murine phenylketonuria (PKU).
Hamman KJ, Winn SR, Harding CO.
Hamman KJ, et al.
Mol Genet Metab. 2011 Nov;104(3):235-40. doi: 10.1016/j.ymgme.2011.07.027. Epub 2011 Aug 4.
Mol Genet Metab. 2011.
PMID: 21917493
Free PMC article.
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